nizubaglustat Verified listing

Indicaton

Has the potential to treat multiple rare lysosomal storage disorders with neurological involvement, including GM1 and GM2 gangliosidoses, and Niemann-Pick type C disease (NPC).

Therapeutic indications

Type of product

Small molecule

Table

Phase

Phase III started
Partnering status

Not partnered
Available in

Global

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nizubaglustat Verified listing

nizubaglustat Verified listing

Indicaton

Therapeutic indications

Type of product

Company

Table

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